Lived experience

Experiences

Accounts from people who have been through gene therapy, and from the people alongside them. Grouped by who is telling the story, because what a parent noticed is not what the patient noticed.

One person's experience, not medical advice. Written by a person describing their own life. It is not clinical guidance and has not been reviewed as such.

Patients own their own words. No one has permission to copy an experience from this site and use it elsewhere. Whose words these are

Talking to a person

Asking for support, and sharing what you have been through, are two different things. Choose the one that fits.

Would you like to speak to someone who has been through it?

A page can only go so far. If you would rather talk to a person, you can ask. You will be contacted first. Nothing is published.

Request a conversation

Share your experience

If you have been through it, you can say how it was, and choose a nickname or your real name to sit with those words. If you are willing to talk to someone who is still deciding, there is a question about whether your contact details may be kept. Nothing is published.

Share your experience